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delivery combined with blood and hematopoietic disease相关文献:
CRISPR/Cas9 beta-globin gene targeting in human haematopoietic stem cells.
Dever DP, Bak RO, Reinisch A, Camarena J, Washington G, Nicolas CE, Pavel-Dinu M, Saxena N, Wilkens AB, Mantri S, Uchida N, Hendel A, Narla A, Majeti R, Weinberg KI, Porteus MH.
Nature. 2016 Nov 17;539(7629):384-389. doi: 10.1038/nature20134. Epub 2016 Nov 7.
PMID:27820943
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease.
Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G, Gross F, Yvon E, Nusbaum P, Selz F, Hue C, Certain S, Casanova JL, Bousso P, Deist FL, Fischer A.
Science. 2000 Apr 28;288(5466):669-72. doi: 10.1126/science.288.5466.669.
PMID:10784449
CRISPR/Cas9-mediated gene editing. A promising strategy in hematological disorders.
Ugalde L, Fañanas S, Torres R, Quintana-Bustamante O, Río P.
Cytotherapy. 2023 Mar;25(3):277-285. doi: 10.1016/j.jcyt.2022.11.014. Epub 2023 Jan 5.
PMID:36610813
Guidelines for the use and interpretation of assays for monitoring autophagy (3rd edition).
Klionsky DJ, Abdelmohsen K, Abe A, Abedin MJ, Abeliovich H, Acevedo Arozena A, Adachi H, Adams CM, Adams PD, Adeli K, Adhihetty PJ, Adler SG, Agam G, Agarwal R, Aghi MK, Agnello M, Agostinis P, Aguilar PV, Aguirre-Ghiso J, Airoldi EM, Ait-Si-Ali S, Akematsu T, Akporiaye ET, Al-Rubeai M, Albaiceta GM, Albanese C, Albani D, Albert ML, Aldudo J, Algül H, Alirezaei M, Alloza I, Almasan A, Almonte-Beceril M, Alnemri ES, Alonso C, Altan-Bonnet N, Altieri DC, Alvarez S, Alvarez-Erviti L, Alves S, Amadoro G, Amano A, Amantini C, Ambrosio S, Amelio I, Amer AO, Amessou M, Amon A, An Z, Anania FA, Andersen SU, Andley UP, Andreadi CK, Andrieu-Abadie N, Anel A, Ann DK, Anoopkumar-Dukie S, Antonioli M, Aoki H, Apostolova N, Aquila S, Aquilano K, Araki K, Arama E, Aranda A, Araya J, Arcaro A, Arias E, Arimoto H, Ariosa AR, Armstrong JL, Arnould T, Arsov I, Asanuma K, Askanas V, Asselin E, Atarashi R, Atherton SS, Atkin JD, Attardi LD, Auberger P, Auburger G, Aurelian L, Autelli R, Avagliano L, Avantaggiati ML, Avrahami L, Awale S, Azad N, Bachetti T, Backer JM, Bae DH, Bae JS, Bae ON, Bae SH, Baehrecke EH, Baek SH, Baghdiguian S, Bagniewska-Zadworna A, Bai H, Bai J, Bai XY, Bailly Y, Balaji KN, …
Autophagy. 2016;12(1):1-222. doi: 10.1080/15548627.2015.1100356.
PMID:26799652
Evidence-based management of primary and secondary CNS lymphoma.
Khwaja J, Nayak L, Cwynarski K.
Semin Hematol. 2023 Nov;60(5):313-321. doi: 10.1053/j.seminhematol.2023.11.003. Epub 2023 Dec 1.
PMID:38135609
Advances in therapies for neurological lysosomal storage disorders.
Ellison S, Parker H, Bigger B.
J Inherit Metab Dis. 2023 Sep;46(5):874-905. doi: 10.1002/jimd.12615. Epub 2023 May 2.
PMID:37078180
Antibody based conditioning for allogeneic hematopoietic stem cell transplantation.
Saha A, Blazar BR.
Front Immunol. 2022 Oct 20;13:1031334. doi: 10.3389/fimmu.2022.1031334. eCollection 2022.
PMID:36341432
Optimization of universal allogeneic CAR-T cells combining CRISPR and transposon-based technologies for treatment of acute myeloid leukemia.
Calviño C, Ceballos C, Alfonso A, Jauregui P, Calleja-Cervantes ME, San Martin-Uriz P, Rodriguez-Marquez P, Martin-Mallo A, Iglesias E, Abizanda G, Rodriguez-Diaz S, Martinez-Turrillas R, Illarramendi J, Viguria MC, Redondo M, Rifon J, Villar S, Lasarte JJ, Inoges S, Lopez-Diaz de Cerio A, Hernaez M, Prosper F, Rodriguez-Madoz JR.
Front Immunol. 2023 Sep 19;14:1270843. doi: 10.3389/fimmu.2023.1270843. eCollection 2023.
PMID:37795087
Bioinspired and Biomimetic Nanomedicines.
Chen Z, Wang Z, Gu Z.
Acc Chem Res. 2019 May 21;52(5):1255-1264. doi: 10.1021/acs.accounts.9b00079. Epub 2019 Apr 12.
PMID:30977635
Robust CAR-T memory formation and function via hematopoietic stem cell delivery.
Zhen A, Carrillo MA, Mu W, Rezek V, Martin H, Hamid P, Chen ISY, Yang OO, Zack JA, Kitchen SG.
PLoS Pathog. 2021 Apr 1;17(4):e1009404. doi: 10.1371/journal.ppat.1009404. eCollection 2021 Apr.
PMID:33793675
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