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Duchenne muscular dystrophy相关文献:
Duchenne muscular dystrophy.
Duan D, Goemans N, Takeda S, Mercuri E, Aartsma-Rus A.
Nat Rev Dis Primers. 2021 Feb 18;7(1):13. doi: 10.1038/s41572-021-00248-3.
PMID:33602943
Therapeutic Strategies for Duchenne Muscular Dystrophy: An Update.
Sun C, Shen L, Zhang Z, Xie X.
Genes (Basel). 2020 Jul 23;11(8):837. doi: 10.3390/genes11080837.
PMID:32717791
Duchenne muscular dystrophy.
Yiu EM, Kornberg AJ.
J Paediatr Child Health. 2015 Aug;51(8):759-64. doi: 10.1111/jpc.12868. Epub 2015 Mar 9.
PMID:25752877
CRISPR-Cas9 Gene Therapy for Duchenne Muscular Dystrophy.
Happi Mbakam C, Lamothe G, Tremblay G, Tremblay JP.
Neurotherapeutics. 2022 Apr;19(3):931-941. doi: 10.1007/s13311-022-01197-9. Epub 2022 Feb 14.
PMID:35165856
Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management.
Birnkrant DJ, Bushby K, Bann CM, Alman BA, Apkon SD, Blackwell A, Case LE, Cripe L, Hadjiyannakis S, Olson AK, Sheehan DW, Bolen J, Weber DR, Ward LM; DMD Care Considerations Working Group.
Lancet Neurol. 2018 Apr;17(4):347-361. doi: 10.1016/S1474-4422(18)30025-5. Epub 2018 Feb 3.
PMID:29395990
Duchenne Muscular Dystrophy: From Diagnosis to Therapy.
Falzarano MS, Scotton C, Passarelli C, Ferlini A.
Molecules. 2015 Oct 7;20(10):18168-84. doi: 10.3390/molecules201018168.
PMID:26457695
[Update on Duchenne muscular dystrophy].
Leiva-Cepas F, Montaño Martínez A, López-López I.
Semergen. 2021 Oct;47(7):472-481. doi: 10.1016/j.semerg.2021.06.008. Epub 2021 Aug 18.
PMID:34417099
Duchenne muscular dystrophy.
Annexstad EJ, Lund-Petersen I, Rasmussen M.
Tidsskr Nor Laegeforen. 2014 Aug 5;134(14):1361-4. doi: 10.4045/tidsskr.13.0836. eCollection 2014 Aug 5.
PMID:25096430
Exercise Training in Duchenne Muscular Dystrophy: A Systematic Review and Meta-Analysis.
Hammer S, Toussaint M, Vollsæter M, Nesbjørg Tvedt M, Drange Røksund O, Reychler G, Lund H, Andersen T.
J Rehabil Med. 2022 Jan 11;54:jrm00250. doi: 10.2340/jrm.v53.985.
PMID:35642324
Therapeutic developments for Duchenne muscular dystrophy.
Verhaart IEC, Aartsma-Rus A.
Nat Rev Neurol. 2019 Jul;15(7):373-386. doi: 10.1038/s41582-019-0203-3.
PMID:31147635
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