Current status of beta-thalassemia and its treatment strategies.
Ali S, Mumtaz S, Shakir HA, Khan M, Tahir HM, Mumtaz S, Mughal TA, Hassan A, Kazmi SAR, Sadia, Irfan M, Khan MA.
Mol Genet Genomic Med. 2021 Dec;9(12):e1788. doi: 10.1002/mgg3.1788. Epub 2021 Nov 5.
beta-Thalassemia.
Origa R.
Genet Med. 2017 Jun;19(6):609-619. doi: 10.1038/gim.2016.173. Epub 2016 Nov 3.
Beta-thalassemia.
Galanello R, Origa R.
Orphanet J Rare Dis. 2010 May 21;5:11. doi: 10.1186/1750-1172-5-11.
Beta-thalassemia.
Cao A, Galanello R.
Genet Med. 2010 Feb;12(2):61-76. doi: 10.1097/GIM.0b013e3181cd68ed.
β-Thalassemias.
Taher AT, Musallam KM, Cappellini MD.
N Engl J Med. 2021 Feb 25;384(8):727-743. doi: 10.1056/NEJMra2021838.
Changing patterns in the epidemiology of beta-thalassemia.
Kattamis A, Forni GL, Aydinok Y, Viprakasit V.
Eur J Haematol. 2020 Dec;105(6):692-703. doi: 10.1111/ejh.13512. Epub 2020 Sep 21.
Challenges of blood transfusions in beta-thalassemia.
Shah FT, Sayani F, Trompeter S, Drasar E, Piga A.
Blood Rev. 2019 Sep;37:100588. doi: 10.1016/j.blre.2019.100588. Epub 2019 Jul 6.
Alpha- and Beta-thalassemia: Rapid Evidence Review.
Baird DC, Batten SH, Sparks SK.
Am Fam Physician. 2022 Mar 1;105(3):272-280.
2021 update on clinical trials in beta-thalassemia.
Musallam KM, Bou-Fakhredin R, Cappellini MD, Taher AT.
Am J Hematol. 2021 Nov 1;96(11):1518-1531. doi: 10.1002/ajh.26316. Epub 2021 Aug 18.
CRISPR/Cas-based gene editing in therapeutic strategies for beta-thalassemia.
Zeng S, Lei S, Qu C, Wang Y, Teng S, Huang P.
Hum Genet. 2023 Dec;142(12):1677-1703. doi: 10.1007/s00439-023-02610-9. Epub 2023 Oct 25.
